RA CAPITAL MANAGEMENT, L.P. — 13F Holdings & Portfolio

CIK 1346824 · latest 13F-HR filed 2026-08-14

RA CAPITAL MANAGEMENT, L.P. manages $11.51B in 13F-reported U.S. long-equity assets across 85 reported positions as of its 2026-06-30 13F-HR filing. Its largest disclosed positions are ASND (23.83%), PBLS (6.88%), RYTM (6.43%). Quarter over quarter (versus its 2026-03-31 filing) the fund opened 17 new positions, exited 18, added to 38, and trimmed 13.

AUM is the long-equity portion reported on Form 13F-HR. Excludes short positions, cash, foreign holdings, and non-13F assets. For informational purposes only — not investment advice.

Filer Information
Address
200 BERKELEY STREET, 18TH FLOOR
BOSTON, MA 02116
Phone
(617) 778-2500
Filing Manager
RA CAPITAL MANAGEMENT, L.P.
BOSTON, MA
Signatory
Rajeev Shah
Authorized Signatory
Loading holdings…
AUM

$11.51B

Long-equity book

Holdings

85

Distinct positions

Period

2026-06-30

Filed 2026-08-14

Q/Q Activity

+17 / −18 / ↑38 / ↓13

vs 2026-03-31

Firm Profile & Key People
Name Title / Status Ownership Type

Top Adds (vs prior quarter)

  • RHYTHM PHARMACEUTICALS INC$160.4M +27.7%
  • ARTIVA BIOTHERAPEUTICS INC$110.7M +174.5%
  • GH RESEARCH PLC$97.3M +90.2%
  • BICARA THERAPEUTICS INC$71.1M +49.3%
  • CLIMB BIO INC$70.0M +90.4%
Show all 38 →

Top Trims

  • NUVALENT INC-A-$105.7M -40.7%
  • TYRA BIOSCIENCES INC-$77.6M -16.6%
  • VOR BIOPHARMA INC-$52.2M -54.1%
  • GERON CORP-$40.2M -42.3%
  • WAVE LIFE SCIENCES LTD-$38.8M -19.9%
Show all 13 →

New Positions

  • ASCENDIS PHARMA A/S$2.74B
  • PARABILIS MEDICINES INC$791.9M
  • HEMAB THERAPEUTICS HOLDINGS$286.8M
  • ABIVAX SA-ADR$150.9M
  • ORUKA THERAPEUTICS INC$148.0M
Show all 17 →

Exited Positions

  • ASCENDIS PHARMA A/S - ADR$2.35B
  • DIANTHUS THERAPEUTICS INC$219.2M
  • PRAXIS PRECISION MEDICINES I$120.4M
  • SAREPTA THERAPEUTICS INC$84.9M
  • SPYRE THERAPEUTICS INC$81.8M
Show all 18 →
All Holdings

Rows tagged Call or Put are options positions, not stock. Per SEC Form 13F-HR, Value shows the notional value of the underlying (shares covered × underlying price), not the option premium. Shares is the number of underlying shares covered (divide by 100 for contract count).

# Issuer Symbol CUSIP Value Weight Shares Type
1 ASCENDIS PHARMA A/S ASND K08588103 $2.74B 23.83% 10,281,496 SH
2 PARABILIS MEDICINES INC PBLS 698955101 $791.9M 6.88% 28,933,371 SH
3 RHYTHM PHARMACEUTICALS INC RYTM 76243J105 $740.2M 6.43% 6,666,837 SH
4 VAXCYTE INC PCVX 92243G108 $667.0M 5.80% 11,474,599 SH
5 SIONNA THERAPEUTICS INC SION 829401108 $435.7M 3.79% 9,905,045 SH
6 TYRA BIOSCIENCES INC TYRA 90240B106 $389.6M 3.39% 12,198,625 SH
7 EDGEWISE THERAPEUTICS INC EWTX 28036F105 $341.0M 2.96% 8,392,730 SH
8 NEWAMSTERDAM PHARMA CO NV NAMS N62509109 $323.7M 2.81% 9,550,191 SH
9 HEMAB THERAPEUTICS HOLDINGS COAG 423494103 $286.8M 2.49% 7,808,627 SH
10 SEPTERNA INC SEPN 81734D104 $234.3M 2.04% 6,995,858 SH
11 BICARA THERAPEUTICS INC BCAX 055477103 $215.4M 1.87% 7,255,993 SH
12 MINERALYS THERAPEUTICS INC MLYS 603170101 $207.6M 1.80% 7,692,750 SH
13 GH RESEARCH PLC GHRS G3855L106 $205.3M 1.78% 7,636,813 SH
14 DISC MEDICINE INC IRON 254604101 $179.2M 1.56% 2,450,221 SH
15 SPYGLASS PHARMA INC SGP 85220G109 $178.6M 1.55% 8,021,117 SH
16 ARTIVA BIOTHERAPEUTICS INC ARTV 04317A107 $174.2M 1.51% 17,955,642 SH
17 JANUX THERAPEUTICS INC JANX 47103J105 $171.9M 1.49% 11,189,693 SH
18 TAYSHA GENE THERAPIES INC TSHA 877619106 $160.4M 1.39% 23,555,648 SH
19 BIOCRYST PHARMACEUTICALS INC BCRX 09058V103 $158.3M 1.38% 15,827,186 SH
20 WAVE LIFE SCIENCES LTD WVE Y95308105 $156.7M 1.36% 26,975,505 SH
21 NUVALENT INC-A NUVL 670703107 $153.9M 1.34% 1,246,456 SH
22 ABIVAX SA-ADR ABVX 00370M103 $150.9M 1.31% 1,132,557 SH
23 ORUKA THERAPEUTICS INC ORKA 687604108 $148.0M 1.29% 1,554,597 SH
24 SOLID BIOSCIENCES INC SLDB 83422E204 $120.2M 1.04% 12,036,126 SH
25 CLIMB BIO INC CLYM 28658R106 $115.0M 1.00% 8,821,067 SH
26 ZAI LAB LTD-ADR ZLAB 98887Q104 $109.1M 0.95% 5,743,533 SH
27 ARS PHARMACEUTICALS INC SPRY 82835W108 $87.0M 0.76% 10,860,977 SH
28 XENCOR INC XNCR 98401F105 $84.9M 0.74% 5,274,274 SH
29 JADE BIOSCIENCES INC JBIO 008064206 $81.6M 0.71% 3,671,083 SH
30 INTELLIA THERAPEUTICS INC NTLA 45826J105 $76.6M 0.67% 4,526,926 SH
31 LB PHARMACEUTICALS INC LBRX 50180M108 $71.7M 0.62% 2,208,604 SH
32 DEFINIUM THERAPEUTICS INC DFTX 24477V105 $70.6M 0.61% 1,500,000 SH
33 ACLARIS THERAPEUTICS INC ACRS 00461U105 $67.3M 0.58% 12,723,026 SH
34 4D MOLECULAR THERAPEUTICS IN FDMT 35104E100 $67.2M 0.58% 5,049,779 SH
35 SANA BIOTECHNOLOGY INC SANA 799566104 $65.4M 0.57% 18,750,000 SH
36 DAMORA THERAPEUTICS INC DMRA 36322Q206 $62.4M 0.54% 2,399,702 SH
37 MONOPAR THERAPEUTICS INC MNPR 61023L207 $61.8M 0.54% 667,207 SH
38 ACUMEN PHARMACEUTICALS INC ABOS 00509G209 $56.1M 0.49% 20,992,669 SH
39 GERON CORP GERN 374163103 $54.8M 0.48% 42,809,751 SH
40 REZOLUTE INC RZLT 76200L309 $49.1M 0.43% 9,445,039 SH
41 EVOMMUNE INC EVMN 30054Y107 $46.4M 0.40% 3,494,638 SH
42 VOR BIOPHARMA INC VOR 929033207 $44.2M 0.38% 2,402,095 SH
43 CENTURY THERAPEUTICS INC IPSC 15673T100 $43.5M 0.38% 17,754,430 SH
44 AKTIS ONCOLOGY INC AKTS 01021M104 $42.4M 0.37% 1,314,405 SH
45 BIOAGE LABS INC BIOA 09077V100 $41.0M 0.36% 1,671,648 SH
46 C4 THERAPEUTICS INC CCCC 12529R107 $37.4M 0.32% 8,000,000 SH
47 MIRUM PHARMACEUTICALS INC MIRM 604749101 $37.3M 0.32% 318,554 SH
48 CAPRICOR THERAPEUTICS INC CAPR 14070B309 $36.3M 0.32% 1,507,844 SH
49 PEPGEN INC PEPG 713317105 $36.1M 0.31% 20,064,545 SH
50 PRELUDE THERAPEUTICS INC PRLD 74065P101 $34.5M 0.30% 6,475,882 SH
Filing History
Period Filed AUM Holdings Accession
2026-06-30 2026-08-14 $11.51B 85 0001104659-26-097251
2026-03-31 2026-05-15 $9.44B 86 0001104659-26-062637
2025-12-31 2026-02-17 $9.76B 72 0001104659-26-016482
2025-09-30 2025-11-14 $8.12B 68 0001104659-25-112469