Palo Alto Investors LP — 13F Holdings & Portfolio

CIK 1306923 · latest 13F-HR filed 2026-08-19

Palo Alto Investors LP manages $723.7M in 13F-reported U.S. long-equity assets across 52 reported positions as of its 2026-06-30 13F-HR filing. Its largest disclosed positions are PTCT (10.36%), ACAD (10.01%), INSM (6.10%). Quarter over quarter (versus its 2026-06-30 filing) the fund opened 1 new position, exited 1, added to 0, and trimmed 0.

AUM is the long-equity portion reported on Form 13F-HR. Excludes short positions, cash, foreign holdings, and non-13F assets. For informational purposes only — not investment advice.

Filer Information
Address
101 UNIVERSITY AVE
SUITE 200
PALO ALTO, CA 94301
Phone
(650) 325-0772
Filing Manager
Palo Alto Investors LP
PALO ALTO, CA
Signatory
Angela Nguyen Dinh
Chief Compliance Officer
Loading holdings…
AUM

$723.7M

Long-equity book

Holdings

52

Distinct positions

Period

2026-06-30

Filed 2026-08-19

Q/Q Activity

+1 / −1 / ↑0 / ↓0

vs 2026-06-30

Firm Profile & Key People
Name Title / Status Ownership Type

Top Adds (vs prior quarter)

  • No increased positions.
Show all 0 →

Top Trims

  • No decreased positions.
Show all 0 →

New Positions

  • MIRUM PHARMACEUTICALS INC$40.8M
Show all 1 →

Exited Positions

  • MIRUM PHARMACEUTICALS INC$40.8M
Show all 1 →
All Holdings

Rows tagged Call or Put are options positions, not stock. Per SEC Form 13F-HR, Value shows the notional value of the underlying (shares covered × underlying price), not the option premium. Shares is the number of underlying shares covered (divide by 100 for contract count).

# Issuer Symbol CUSIP Value Weight Shares Type
1 PTC THERAPEUTICS INC PTCT 69366J200 $75.0M 10.36% 918,846 SH
2 ACADIA PHARMACEUTICALS INC ACAD 004225108 $72.5M 10.01% 2,864,096 SH
3 INSMED INC INSM 457669307 $44.1M 6.10% 413,980 SH
4 MIRUM PHARMACEUTICALS INC MIRM 604749101 $40.8M 5.64% 348,808 SH
5 ANAPTYSBIO INC ANAB 032724106 $40.7M 5.63% 603,489 SH
6 BIOMARIN PHARMACEUTICAL INC BMRN 09061G101 $39.1M 5.40% 682,777 SH
7 DYNE THERAPEUTICS INC DYN 26818M108 $36.6M 5.06% 1,647,521 SH
8 UNITED THERAPEUTICS CORP UTHR 91307C102 $33.9M 4.69% 62,587 SH
9 DISC MEDICINE INC IRON 254604101 $30.5M 4.21% 416,646 SH
10 BIOGEN INC BIIB 09062X103 $30.3M 4.19% 140,279 SH
11 IOVANCE BIOTHERAPEUTICS INC IOVA 462260100 $22.0M 3.04% 5,296,209 SH
12 ULTRAGENYX PHARMACEUTICAL IN RARE 90400D108 $19.9M 2.75% 596,495 SH
13 NOVOCURE LTD NVCR G6674U108 $19.4M 2.68% 1,280,439 SH
14 SYNDAX PHARMACEUTICALS INC SNDX 87164F105 $18.9M 2.61% 864,986 SH
15 ANNEXON INC ANNX 03589W102 $16.8M 2.33% 2,948,090 SH
16 BICARA THERAPEUTICS INC BCAX 055477103 $16.3M 2.26% 550,408 SH
17 CAREDX INC CDNA 14167L103 $15.2M 2.09% 531,870 SH
18 CELLDEX THERAPEUTICS INC CLDX 15117B202 $14.9M 2.06% 399,856 SH
19 COMPASS THERAPEUTICS INC CMPX 20454B104 $12.8M 1.76% 5,831,813 SH
20 ALKERMES PLC ALKS G01767105 $12.7M 1.76% 242,560 SH
21 FIRST TRACKS BIOTHERAPEUTICS TRAX 337185102 $12.1M 1.68% 603,489 SH
22 PROTHENA CORP PLC PRTA G72800108 $11.2M 1.55% 1,143,155 SH
23 TRAVERE THERAPEUTICS INC TVTX 89422G107 $9.5M 1.32% 167,525 SH
24 TAYSHA GENE THERAPIES INC TSHA 877619106 $9.5M 1.31% 1,391,382 SH
25 ACLARIS THERAPEUTICS INC ACRS 00461U105 $8.5M 1.18% 1,613,430 SH
26 AGIOS PHARMACEUTICALS INC AGIO 00847X104 $7.9M 1.10% 213,601 SH
27 CAPRICOR THERAPEUTICS INC CAPR 14070B309 $5.5M 0.76% 229,763 SH
28 ALIGN TECHNOLOGY INC ALGN 016255101 $5.3M 0.73% 31,389 SH
29 ORUKA THERAPEUTICS INC - Restricted ORKA 687604108 $3.2M 0.44% 33,546 SH
30 XENON PHARMACEUTICALS INC XENE 98420N105 $3.1M 0.43% 51,345 SH
31 NEUROCRINE BIOSCIENCES INC NBIX 64125C109 $3.1M 0.42% 18,117 SH
32 EDWARDS LIFESCIENCES CORP EW 28176E108 $3.0M 0.42% 33,640 SH
33 STOKE THERAPEUTICS INC STOK 86150R107 $2.8M 0.38% 84,631 SH
34 CYTOKINETICS INC CYTK 23282W605 $2.7M 0.38% 32,195 SH
35 PYXIS ONCOLOGY INC PYXS 747324101 $2.6M 0.36% 864,277 SH
36 EHEALTH INC EHTH 28238P109 $2.2M 0.31% 1,482,797 SH
37 CRISPR THERAPEUTICS AG CRSP H17182108 $2.2M 0.30% 39,605 SH
38 SAGIMET BIOSCIENCES INC-A SGMT 786700104 $1.9M 0.27% 250,000 SH
39 NUVATION BIO INC NUVB 67080N101 $1.9M 0.26% 326,609 SH
40 BIONTECH SE-ADR BNTX 09075V102 $1.8M 0.25% 19,614 SH
41 COMPASS PATHWAYS PLC ADR CMPS 20451W101 $1.6M 0.23% 115,616 SH
42 HUMANA INC HUM 444859102 $1.6M 0.22% 3,985 SH
43 NEWAMSTERDAM PHARMA CO NV NAMS N62509109 $1.5M 0.21% 44,359 SH
44 VERASTEM INC VSTM 92337C203 $1.2M 0.16% 309,685 SH
45 MADRIGAL PHARMACEUTICALS INC MDGL 558868105 $959.5K 0.13% 1,787 SH
46 UROGEN PHARMA LTD URGN M96088105 $901.6K 0.12% 24,500 SH
47 BICYCLE THERAPEUTICS PLC-ADR BCYC 088786108 $856.0K 0.12% 201,890 SH
48 XERIS BIOPHARMA HOLDINGS INC XERS 98422E103 $826.9K 0.11% 104,410 SH
49 ABEONA THERAPEUTICS INC ABEO 00289Y206 $672.8K 0.09% 108,865 SH
50 INSPIRE MEDICAL SYSTEMS INC INSP 457730109 $391.3K 0.05% 8,772 SH
Filing History
Period Filed AUM Holdings Accession
2026-06-30 2026-08-18 $723.7M 52 0002073679-26-000101
2026-06-30 2026-08-17 $723.7M 52 0002073679-26-000096
2026-06-30 2026-08-19 $723.7M 52 0002073679-26-000102
2026-03-31 2026-05-15 $653.9M 51 0001306923-26-000004
2025-12-31 2026-02-17 $718.4M 49 0001306923-26-000002
2025-09-30 2025-11-14 $540.4M 44 0001306923-25-000019